WOODBRIDGE – A fundraiser to benefit brave 4-year-old township resident Scarlett Griffith and heighten awareness about the ...

Gio passed away a couple of years ago from a rare genetic condition called Morquio A syndrome. He spent quite a few months at ...

In 2015, NICE said that BioMarin's Vimizim could be used to treat patients with the ultra-rare disease Morquio A syndrome, while real-world data was collected on its efficacy. Now – almost seven ...

Monday marks the 129th Boston Marathon, with more than 200 Mainers among the 30,000-plus runners in the field.However, not ...

Its initial targets are Gaucher disease, Morquio syndrome (also called mucopolysaccharidosis type IV), GM1 gangliosidosis (GM1) and Parkinson’s disease. The company has developed a toolkit ...

Living with a rare condition like Morquio Syndrome presents unique hurdles. Yet, my journey has turned adversity into a force for positive change and healthcare advocacy. Graduating with a BA in ...

All proceeds from Scarlett’s Mini Golf Gala will directly support Scarlett’s ongoing medical care and research toward developing a cure for Morquio A Syndrome, which affects just four in 1 ...