LHON is a rare mitochondrial disease that affects around two in 100,000 people across Europe, and usually leaves sufferers registered blind within months of the first symptoms 1. Onset is ...

describing LHON as “like having a flashlight in the centre of your vision all the time, night and day”. The rare disorder, which leaves 80% of patients legally blind within one year ...

Lenadogene nolparvovec, an adeno-associated virus (AAV)-based gene therapy, was developed to address LHON and has been ...