Krystie Maddox, 12, who lives in Wolverhampton with her mother Molvia, 40, a business consultant and stepfather Mitchell, 34, also a consultant, has Friedreich's Ataxia, a rare inherited disorder ...
citing an "asymmetric" risk/reward ahead of regulatory updates for its drug candidate nomla for Friedreich’s ataxia, or FA. The investment bank noted that concerns about nomla's safety and ...
An experimental gene therapy developed by Lexeo Therapeutics has shown early promise in treating one of the most serious complications of the rare neurodegenerative disorder, Friedreich's ataxia (FA).
Editor’s note: This is an automatically generated transcript, which has been slightly edited for clarity. Please notify [email protected] if there are concerns regarding accuracy of the ...
After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU.
In this video David Lynch, MD, PhD, highlights one of the greatest unmet needs in Friedreich's ataxia management.
Dunlavin was alive with the sounds of music and song when the community came together at St Nicholas Church of Ireland for a ...
Offering insight into the progression of the disease and how it has affected her daughters, former Dunlavin GP, Mary Kearney, who now works at the National Ataxia Centre at Tallaght University ...